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@WORLDSymposia Profile picture

WORLDSymposia

@WORLDSymposia

We're Organizing Research on Lysosomal Diseases

Joined September 2014
843Posts 950Followers 370Following
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WORLDSymposia Profile Picture
WORLDSymposia
 @WORLDSymposia
27 Nov

Late-breaking Abstract Submission closing next Monday, Dec. 2 - Only 5 days left to submit late-breaking abstracts and last chance to have platform presentation at WORLDSymposium 2025. Visit worldsymposia.org/worldsymposium… to submit your abstracts today! #WORLDSymposia #LysosomalDisease

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WORLDSymposia
 @WORLDSymposia
20 Nov

Congratulations to the ten individuals selected to receive the WORLDSymposium 2025 Young Investigator Award. Visit worldsymposia.org/worldsymposium… to see the list of award recipients. #WORLDSymposia #RareDiseases #CareAboutRare

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WORLDSymposia
 @WORLDSymposia
4 Nov

Please Share: WORLDSymposium 2025 Late-breaking Call for Abstracts Now Open. #WORLDSymposia will be accepting late-breaking abstracts from Nov. 1 to Dec. 2, 2024 for poster presentation & possible platform presentation. More at worldsymposia.org/worldsymposium… #RareDisease #CareAboutRare

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WORLDSymposia
 @WORLDSymposia
1 Nov

WORLDSymposium announces James M. Wilson, MD, PhD, President and CEO of GEMMA Biotherapeutics, to receive the 2025 Roscoe O. Brady Award on Tuesday, February 4, 2025 at 08:00 PST. worldsymposia.org/worldsymposium… #WORLDSymposia #RareDisease #CareAboutRare

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WORLDSymposia
 @WORLDSymposia
23 Oct

Congratulations to Maria Kefalas, co-founder of the Calliope Joy Foundation and Dean and Teryn Suhr, co-founders of the MLD Foundation. All to receive the PAL Award at WORLDSymposium 2025 on Wed, Feb 5, 2025 #WORLDSymposia #RareDiseases #careaboutrare tinyurl.com/ym4p5nn9

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WORLDSymposia
 @WORLDSymposia
30 Sep

WORLDSymposium 2025 abstract submission closes tomorrow - Only 1 day left to submit an abstract and the last chance to have abstract included in the February MGM Journal. Visit worldsymposia.org/worldsymposium… to submit your abstracts today! #WORLDSymposia #CareAboutRare #LysosomalDisease

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Abstract Submissions - WORLDSymposium
Source: https://t.co/xXZCUFmqjK
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WORLDSymposia
 @WORLDSymposia
27 Sep

WORLDSymposium is pleased to announce Peter Marks, MD, PhD, will present the Keynote Address on Thursday, February 6, 2025 at the 21st Annual WORLDSymposium in San Diego, CA. #WORLDSymposia #RareDiseases #careaboutrare worldsymposia.org/worldsymposium…

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WORLDSymposia
 @WORLDSymposia
13 Sep

Introducing SPOTLIGHT - a monthly feature dedicated to advancing the understanding of lysosomal diseases. The inaugural focus: mucopolysaccharidoses (MPS). Explore recent breakthroughs & join the scientific discourse. worldsymposia.org/september-2024… #LysosomalDisease #MPS #WORLDSymposia

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WORLDSymposia
 @WORLDSymposia
27 Aug

CLOSING IN SEVEN DAYS: Nominations for the 2025 Roscoe O. Brady, PAL & Catalyst Awards: worldsymposia.org/worldsymposium… DEADLINE: Tuesday, September 3, 2024 at 23:59 CDT. #WORLDSymposia #CareAboutRare #RareDisease

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WORLDSymposia
 @WORLDSymposia
12 Feb

Giacomo Chiesi, Head of Chiesi GRD, accepted a 2024 #WORLDSymposium New Treatment Award for velmanase alfa-tycv (Lamzede®), the first US ERT approved for non-CNS manifestations of #AlphaMannosidosis in adults and pediatric patients tinyurl.com/2p8b5uuc #LysosomalDisease

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WORLDSymposia
 @WORLDSymposia
12 Feb

Diego Ardigo, Head of Global Research & Development of Chiesi Group, accepted a 2024 #WORLDSymposium New Treatment Award for Elfabrio® — an approved, safe, and effective ERT for adults with #FabryDisease. Learn more: tinyurl.com/2p8b5uuc #RareDiseases #LysosomalDisease

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WORLDSymposia
 @WORLDSymposia
12 Feb

Bradley Campbell, CEO of Amicus Therapeutics, accepted a 2024 #WORLDSymposium New Treatment Award for the two-component therapy of cipaglucosidase alfa (Pombiliti®) and miglustat (Opfolda®) tinyurl.com/2p8b5uuc #RareDiseases #LysosomalDisease #CareAboutRare

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WORLDSymposia
 @WORLDSymposia
9 Feb

Marking its 20th anniversary, #WORLDSymposium 2024 is celebrating significant milestones and special memories from the past two decades with a commemorative video. #RareDiseases #LysosomalDisease #CareAboutRare youtu.be/vWuq2Pqxxec

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WORLDSymposia
 @WORLDSymposia
7 Feb

Congratulations to Alan Finglas, the recipient of the #WORLDSymposium 2024 Patient Advocate Leader Award! Alan's unwavering determination & practical approach have been instrumental in transforming MSD research. #RareDiseases #LysosomalDisease youtu.be/WCRCkkWYuiA

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WORLDSymposia
 @WORLDSymposia
7 Feb

Elsa Shapiro received the 2024 Roscoe O. Brady Award at #WORLDSymposium on Feb 5. Dr. Shapiro is renowned for groundbreaking work in neurocognitive development measurement. Congratulations, Dr. Shapiro! #RareDiseases #LysosomalDisease #CareAboutRare youtu.be/yQ0nwySIZEc

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WORLDSymposia
 @WORLDSymposia
6 Feb

#WORLDSymposia celebrated a pivotal moment, presenting the inaugural "Catalyst" award to Zachary Thomas. Because of his efforts, The Zachary Thomas Newborn Screening Act will be introduced to the Alabama state legislature this week. #RareDiseases #LysosomalDisease #CareAboutRare

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WORLDSymposia
 @WORLDSymposia
12 Jan

NEW in 2024, WORLDSymposium will present the first "Catalyst" award to Zachary Thomas, an incredible rare disease policy advocate, at the Be The Catalyst Event at 6:00 PM PST on February 4, 2024. worldsymposia.org/catalyst-award/ #CareAboutRare #LysosomalDisease #RareDisease

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WORLDSymposia
 @WORLDSymposia
10 Jan

#WORLDSymposia 2024 Speed Mentoring Event: A fantastic way to connect with incredible lysosomal disease leaders in a fun and casual setting. LAST CHANCE: Speed Mentoring sign-up closes TODAY #CareAboutRare #LysosomalDisease #RareDiseases worldsymposia.org/?p=14728

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WORLDSymposia
 @WORLDSymposia
5 Jan

#WORLDSymposia Poster List Now Online. Over 450 abstracts will be presented at four WORLDSymposium 2024 poster sessions. Excellent opportunity to see, hear and discuss specific research topics directly with the abstract authors. worldsymposia.org/?p=94

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PRISMS, Inc.

@smsprisms
501c3 nonprofit - Mission: Advocate for & fund research directed toward a cure or treatment options for children with Sanfilippo Syndrome. Video at https://t.co/0WOT6g9S6G

Cure Sanfilippo Fdn

@CureSanfilippoF
TREND Community is a digital health company using artificial intelligence to capture current perspectives of rare communities from their social data streams.

TREND Community

@trendcommunity
Tweets by Christine White, President. #raredisease @NGFCanada

Christine

@ChristineWNGF

jayne gershkowitz

@jgersh1115
Director Jumpstart Program at Orphan Disease Center University of Pennsylvania

Deborah V. Requesens

@dvrequesens
United States Trends
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